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Yoon, Sea Young, Hunter, Jacqueline E, Chawla, Sanjeev, Clarke, Dana L, Molony, Caitlyn, O'Donnell, Patricia A, Bagel, Jessica H, Kumar, Manoj, Poptani, Harish ORCID: 0000-0002-0593-3235, Vite, Charles H et al (show 1 more authors)
(2020)
Global CNS correction in a large brain model of human alpha-mannosidosis by intravascular gene therapy.
BRAIN, 143 (7).
pp. 2058-2072.