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Ramanan, AV, Hampson, LV, Lythgoe, H, Jones, AP, Hardwick, B, Hind, H, Jacobs, B, Vasileiou, D, Wadsworth, I, Ambrose, N
et al (show 11 more authors) (2019) Defining consensus opinion to develop randomised controlled trials in rare diseases using Bayesian design: An example of a proposed trial of adalimumab versus pamidronate for children with CNO/CRMO. PLOS ONE, 14 (6). e0215739-.

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