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Ramanan, AV, Hampson, LV, Lythgoe, H, Jones, AP, Hardwick, B, Hind, H, Jacobs, B, Vasileiou, D, Wadsworth, I, Ambrose, N et al (show 11 more authors)
(2019)
Defining consensus opinion to develop randomised controlled trials in rare diseases using Bayesian design: An example of a proposed trial of adalimumab versus pamidronate for children with CNO/CRMO.
PLOS ONE, 14 (6).
e0215739-.