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Ranganath, Lakshminarayan R, Psarelli, Eftychia Eirini ORCID: 0000-0002-3102-0288, Arnoux, Jean-Baptiste, Braconi, Daniela, Briggs, Michael, Broijersen, Anders, Loftus, Nadia, Bygott, Helen, Cox, Trevor F, Davison, Andrew S ORCID: 0000-0001-5501-4475 et al (show 39 more authors)
(2020)
Efficacy and safety of once-daily nitisinone for patients with alkaptonuria (SONIA 2): an international, multicentre, open-label, randomised controlled trial.
The Lancet Diabetes and Endocrinology, 8 (9).
pp. 762-772.
Ranganath, Lakshminarayan R, Milan, Anna M ORCID: 0000-0002-0452-2338, Hughes, Andrew T, Khedr, Milad ORCID: 0000-0002-4998-2397, Davison, Andrew S ORCID: 0000-0001-5501-4475, Shweihdi, Ella, Norman, Brendan P ORCID: 0000-0001-9293-4852, Hughes, Juliette H ORCID: 0000-0001-6155-4136, Bygott, Helen, Luangrath, Emily et al (show 20 more authors)
(2020)
Homogentisic acid is not only eliminated by glomerular filtration and tubular secretion but also produced in the kidney in alkaptonuria.
JOURNAL OF INHERITED METABOLIC DISEASE, 43 (4).
pp. 737-747.
Imrich, Richard, Sedlakova, Jana, Ulehlova, Maria, Gornall, Matthew, Jackson, Richard, Olsson, Birgitta, Rudebeck, Mattias, Gallagher, James, Lukacova, Ol'ga, Mlynarikova, Vanda et al (show 10 more authors)
(2022)
Radiological evolution of spinal disease in alkaptonuria and the effect of nitisinone.
RMD OPEN, 8 (2).
e002422-.