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Rosenfeld, Margaret, Cunningham, Steve, Harris, William T, Lapey, Allen, Regelmann, Warren E, Sawicki, Gregory S, Southern, Kevin W ORCID: 0000-0001-6516-9083, Chilvers, Mark, Higgins, Mark, Tian, Simon et al (show 2 more authors)
(2019)
An open-label extension study of ivacaftor in children with CF and a <i>CFTR</i> gating mutation initiating treatment at age 2-5 years (KLIMB).
JOURNAL OF CYSTIC FIBROSIS, 18 (6).
pp. 838-843.